BioPharma Dive1d
How a Biogen drug set the stage for a new biotech targeting ALS
Trace Neuroscience, which launched this week with $101 million, benefited from last year’s approval of Qalsody. Its CEO spoke ...
dermatologyadvisor1d
Gene Therapy for Recessive Dystrophic Epidermolysis Bullosa Under Review
The FDA has accepted for review the resubmitted BLA for prademagene zamikeracel for recessive dystrophic epidermolysis bullosa.
BioPharma Dive1d
Halozyme bids for Evotec; BeiGene gets a new name
The San Diego biotech made an unsolicited bid to buy Evotec for 2 billion euros. Elsewhere, Bluebird recorded its first ...
The American Journal of Managed Care1d
Delandistrogene Moxeparvovec Fails to Meet Primary Endpoint in Phase 3 Study
Put up against placebo in the phase 3 EMBARK trial, delandistrogene moxeparvovec (Elevidys) did not significantly improve ...
Nature16d
Gene therapy articles from across Nature Portfolio
Gene therapy involves the introduction of new genes into cells, to restore or add gene expression, for the purpose of treating disease. Most commonly a mutated gene is replaced with DNA encoding a ...
Yahoo18d
Struggling with mental health, many turn to AI like ChatGPT for therapy
As a person who “reads all the therapy books,” she said, “I haven’t really seen it be wrong.” Anxious, depressed or just lonely, people who can’t find or afford a professional ...
The Washington Post22d
Despite uncertain risks, many turn to AI like ChatGPT for mental health
As a person who “reads all the therapy books,” she said, “I haven’t really seen it be wrong.” Anxious, depressed or just lonely, people who can’t find or afford a professional ...
Business Insider22d
Anna Kendrick says couples therapy didn't help her relationship. Here's how to know when to find a new therapist.
Anna Kendrick didn't have a good experience in couples therapy. On Wednesday's episode of Alex Cooper's "Call Her Daddy" podcast, the "Pitch Perfect" star said she was in a 7-year relationship ...
News Medical22d
Single treatment with CRISPR gene editing therapy offers hope for hereditary angioedema patients
A single treatment with, a CRISPR-Cas9 based gene editing therapy, is enough to replace the daily medication of patients with hereditary angioedema (HAE), a condition characterized by severe ...
Seeking Alpha23d
Intellia slips after mid-stage data for CRISPR-based hereditary angioedema therapy
Intellia Therapeutics (NASDAQ:NTLA) fell ~9% in the pre-market on Thursday after the biotech announced data from an ongoing Phase 2 trial for NTLA-2002, a CRISPR-based gene editing therapy for an ...
FierceBiotech23d
Roche bets up to $1B to expand Dyno gene therapy delivery pact
After forming a gene therapy partnership with Dyno Therapeutics in 2020, Roche is back for more. In a new deal potentially worth more than $1 billion, Roche is paying Dyno $50 million upfront to ...
Medical Xpress23d
CRISPR-Cas9 gene editing trial results support further development as treatment for hereditary angioedema
A single treatment with a CRISPR-Cas9 based gene editing therapy is enough to replace the daily medication of patients with hereditary angioedema (HAE), a condition characterized by severe ...