Adam Feuerstein is a senior writer and biotech columnist, reporting on the crossroads of drug development, business, Wall Street, and biotechnology. He is also a co-host of the weekly biotech podcast ...

Duchenne muscular dystrophy affects about 1 in 3,500 male births globally. Muscle weakness in hips, pelvis, and legs is an early warning sign By age 12, most kids with DMD lose their ability to walk ...

Duchenne muscular dystrophy (DMD) is a genetic disease in which muscle cells fail to produce a protein called dystrophin. Unlike some other forms of muscular dystrophy, in Duchenne there is a complete ...

Duchenne muscular dystrophy (DMD) is a genetic condition that causes progressive muscle weakness and wasting. It is an X-linked recessive disorder that occurs due to changes in the DMD gene, which ...

A recent clinical trial has shown that cellular therapy is safe and effective in stopping the deterioration of upper limb and heart functions in patients with late-stage Duchenne muscular dystrophy. A ...

PARAMUS, N.J., Sept. 19, 2025 /PRNewswire/ -- NS Pharma, Inc. announced today that the U.S. Food & Drug Administration (FDA) has granted Orphan Drug Designation to NS-051/NCNP-04 which is being ...

In an infusion bay at UPMC Children’s Hospital of Pittsburgh, Billy Ellsworth twists the plastic top off of a bottle of Gatorade. “That was kind of tough, to be honest,” he said. “I wasn’t sure I was ...

Lousin Mehrabi is a negotiation professional, inspirational speaker, trainer and advisor in negotiations, emotional intelligence and leadership. She is also the mother of Alex, 11, who has Duchenne ...

Managing osteoporosis and bone health in Duchenne muscular dystrophy occurs in a high-risk environment for fractures due to disease-related loss of muscle and movement, adverse effects of ...

A clinical trial at UC Davis Health and six other sites showed that a cellular therapy offers promise for patients with late-stage Duchenne muscular dystrophy (DMD), a rare genetic disorder causing ...